Spinal muscular atrophy, a disease the author of the article suffers, is one of the genetic diseases with the highest associated mortality. It is also the most expensive to cure.
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Articles on Spinal muscular atrophy
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Spinal muscular dystrophy affects at least 1 in 10,000 people, but new drugs have given hope to those suffering from this rare disease.
A new type of drug blocks the destruction of neurons in the eye, preventing blindness. The researchers hope that the same therapy can be applied to other common neurodegenerative diseases.
It seems like a no brainer to edit out genetic disease…until we pause to consider what would be lost.
